🔬 Current Disease Focus:
Task Progress: 0%
👥 Active Problem Solvers
0
🌍 Experts collaborating globally
⚡ Current Task Assignment
🧬 Genetic Analysis
🔄 Matching experts to specific tasks
📊 Resource Allocation by Research Phase:
📚 Data Analysis
🧪 Experimental Design
🔬 Clinical Trials
💊 Treatment Development
An 18-month double-blind, randomized, placebo-controlled, multicenter, Phas...
Status
Active Not Recruiting
Location
UCSF Children's Hospital and Research Center at Oakland
Start Date
2025-06-30
Trial ID
NCT07082543
LYS-GM101 is a gene therapy for GM1 gangliosidosis intended to deliver a fu...
Status
Terminated
Location
Children's Hospital of Orange County (CHOC)
Start Date
2021-05-11
Trial ID
NCT04273269
Treatments Being Tested
The purpose of this study is to demonstrate that treatment with BMS-986012 ...
Status
Completed
Location
Local Institution - 0075
Start Date
2021-03-17
Trial ID
NCT04702880
Treatments Being Tested
This study is being conducted to better understand the natural course of GM...
Status
Completed
Location
Ann & Robert H. Lurie Children's Hospital of Chicago
Start Date
2019-07-31
Trial ID
NCT04470713
Hypothesis: To characterize and describe disease progression and heterogene...
Status
Recruiting
Location
University of Minnesota - Pediatric Genetics and Metabolism
Start Date
2010-12
Trial ID
NCT00668187
An 18-month double-blind, randomized, placebo-controlled, multicenter, Phas...
Status
Recruiting
Location
UCSF Children's Hospital and Research Center at Oakland
Start Date
2025-06-30
Trial ID
NCT07054515
Background: GM1 gangliosidosis is a disorder that destroys nerve cells. It...
Status
Recruiting
Location
National Institutes of Health Clinical Center
Start Date
2019-08-19
Trial ID
NCT03952637
Treatments Being Tested
This study is designed to test the ability to achieve donor hematopoietic e...
Status
Completed
Location
Masonic Cancer Center, University of Minnesota
Start Date
2012-07-11
Trial ID
NCT01626092
The purpose of this trial is to examine the short term effects (24 Weeks) o...
Status
Completed
Location
Parkinson's Disease Research Unit, Thomas Jefferson University
Start Date
1999-11
Trial ID
NCT00037830
Treatments Being Tested
Owing to the rarity, severity, speed of progression and fatal prognosis of ...
Status
Completed
Location
UCSF Benioff Children's Hospital Oakland
Start Date
2020-06-12
Trial ID
NCT04041102